June live discussion: follistatin gene therapy trial

Just got this email notice from TMA: get your questions ready for the next live discussion!

Remember: this live discussion is at NOON (12PM) Mountain time on June 10th.

BTW: the hyperlinks aren’t working from the email version, to join TMA click here, to view the Live Discussion page click here.

Follistatin Gene Therapy Trial for IBM
Live Discussion

Drs. Jerry Mendell and Brian Kaspar answer your questions about the follistatin gene therapy trial for IBM. June 10, 2013,
2 pm. ET.

Drs. Jerry Mendell and Brian Kaspar are investigators in the follistatin gene therapy trial for inclusion-body myositis patients now underway at Nationwide Children’s Hospital. Several IBM patients have been treated, along with a number of Becker muscular dystrophy patients. Results in the Becker muscular dystrophy patients are encouraging, and show promise for sIBM patients. The Becker patients received a slightly higher dose of the treatment than the first sIBM patients. The results in the Becker patients might allow the next 6 sIBM patients to be treated with the highest dose of the treatment. This should produce better results in the sIBM patients as well. Approval is now being sought from federal regulatory bodies to allow the higher dose treatment. This historic treatment, pioneered in both mice and non-human primates with simulated sIBM, has prompted many questions from IBM patients. Now’s your chance to ask them, as Drs. Mendell and Kaspar both join TMA for a live discussion.

Next live discussion – July 17: Dr. Victoria Werth, professor of dermatology at the University of Pennsylvania, answers your questions about skin care.

TMA members are invited to submit questions in advance of the chat.Click here to submit your questions early.

You MUST be logged in to submit a question.  To login go to www.myositis.org.  Sign in is at the right hand corner.

When submitting questions, please be as brief as possible.  If you have more than one question, submit them separately in the question window.  Questions that are off-topic will not be answered.

Live discussions are a benefit of membership in TMA.  If you’re not already a member, Become a TMA member today to take advantage of Q & A sessions as well as many other member benefits.  Membership is free.

The discussion transcript will be available immediately following the Q & A session.  Visit the Live Discussion page under Community on the TMA homepage to view a complete list of past transcripts and upcoming discussions.

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